Flash, this isn't Trofinetide - came across this page just before and whilst it's a drug to treat retts it's a completely different MOA
This medicine, also known as OAV201, is an adeno-associated virus 9 (AAV9) vector (carrier) for the normal human MECP2 gene. Once injected, the AAV9 vector carrying the normal form of MECP2 releases the gene into the cells. By restoring a normal copy of the MECP2 gene, this medicine is expected to restore the normal functioning of nerve cells and relieve the symptoms of patients with Rett syndrome.The type of virus used in this medicine ('adeno-associated virus') does not cause disease in humans.
A personalised tool to help users track selected stocks. Delivering real-time notifications on price updates, announcements, and performance stats on each to help make informed investment decisions.
(20min delay)