Axo ant given go ahead to treat further patient using AAv silence and replace ????
https://www.globenewswire.com/news-release/2019/11/18/1948616/0/en/Axovant-Gene-Therapies-Receives-Orphan-Drug-Designation-from-FDA-for-AXO-AAV-GM1-for-the-Treatment-of-GM1-Gangliosidosis.html
not to be used please do your own research