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Ann: FDA Grants Orphan Drug Designation for Revascor, page-240

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    Hi Reg,

    yep, I prefer your higher numbers too. Agree re adult dosage being higher - remember, we're going to do an end-run on Ruxolitinib with an inclusion criteria that requires failure of at least one approved therapy & NIH/ BMT CTN seem OK with the restriction.

    Cheers
 
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