from Today's $tockhead !
PYC Therapeutics gets FDA approval
PYC Therapeutics (ASXYC) has received an Orphan Drug Designation (ODD) from the US FDA for its drug candidate, PYC-001, aimed at treating OPA1-associated vision loss.
The ODD is a special designation given to drugs targeting rare diseases. It comes with perks like tax credits for clinical trials, exemptions from certain regulatory fees, and the possibility of market exclusivity for up to 7 years post-approval.
PYC’s investigational drug candidate, PYC-001, is said to be a significant advancement in precision therapy.
The drug was designed to restore the expression of the OPA1 gene to levels necessary for optimal retinal function.
Utilising PYC’s proprietary drug delivery technology, the company has tackled a major hurdle for RNA drugs by ensuring effective delivery to the targeted cells affected by ADOA ( Autosomal Dominant Optic Atrophy).
ADOA is a progressive and irreversible blinding eye disease. It affects approximately 1 in every 35,000 people representing a market size of ~$2 billion per annum.
ADOA stems from a mutation in one copy of the OPA1 gene, which results in inadequate levels of OPA1 gene expression, impacting the normal function of retinal ganglion cells.
The resulting cellular stress and eventual cell death disrupt the transmission of visual signals from the retina to the brain, ultimately causing vision loss in ADOA patients.
- Forums
- ASX - By Stock
- FDA orphan designation
from Today's $tockhead ! PYC Therapeutics gets FDA approval PYC...
-
- There are more pages in this discussion • 4 more messages in this thread...
You’re viewing a single post only. To view the entire thread just sign in or Join Now (FREE)
Featured News
Add PYC (ASX) to my watchlist
|
|||||
Last
13.5¢ |
Change
0.005(3.85%) |
Mkt cap ! $629.9M |
Open | High | Low | Value | Volume |
13.0¢ | 13.5¢ | 12.5¢ | $300.8K | 2.278M |
Buyers (Bids)
No. | Vol. | Price($) |
---|---|---|
1 | 229738 | 13.0¢ |
Sellers (Offers)
Price($) | Vol. | No. |
---|---|---|
13.5¢ | 536997 | 4 |
View Market Depth
No. | Vol. | Price($) |
---|---|---|
1 | 229738 | 0.130 |
5 | 691172 | 0.125 |
10 | 724679 | 0.120 |
3 | 370001 | 0.115 |
9 | 578180 | 0.110 |
Price($) | Vol. | No. |
---|---|---|
0.135 | 536997 | 4 |
0.140 | 1372313 | 6 |
0.145 | 600000 | 1 |
0.150 | 629953 | 6 |
0.165 | 5000 | 1 |
Last trade - 16.10pm 28/08/2024 (20 minute delay) ? |
Featured News
PYC (ASX) Chart |
The Watchlist
HAR
HARANGA RESOURCES LIMITED.
Peter Batten, MD
Peter Batten
MD
Previous Video
Next Video
SPONSORED BY The Market Online