This is a desperate one of, and not clinically trialled but worked DNA treatment for one little girl. newscientist "Molecular scissors
Conventional gene therapy can only be used to add genes to DNA. But with gene editing, specific DNA sequences can be cut with “molecular scissors”, introducing mutations that disable a particular gene. Qasim’s molecular scissors were of a kind known as TALEN proteins."
"Layla will continue to have regular tests until her doctors are sure the cancer is gone. “It is too early to say she is cured,” says Samarasinghe, but she is alive and well.
Cellectis plans to start full clinical trials early in 2016. Qasim says other patients in the UK are already being treated with these cells, although he would not reveal any details. The team will present the case study at the American Society of Hematology meeting in Florida in December.
We will have to wait for the results of those trials to be sure this was not a one-off, but if they are successful, it would be a huge step forward for treating leukaemia and other cancers, Qasim says. “It’s incredibly encouraging,” he says. “There are a whole bunch of other disorders we can now create fixes for.”"
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